Explaining and Improving Efficacy of targeted Immunodeficiency Virus-like Particle Vaccines against AIDS (TIP-VAC)

 

 

Objectives

With support from two successive, framework V, EU sponsored consortia, we have developed a targeted immunodeficiency virus-like particle vaccine (VLP) which has the G-protein of vesicular stomatitis virus incorporated in the membrane of the particle. Incorporation of VSV-G increases uptake and presentation of VLPs by dendritic cells. A pilot vaccination experiment in the SIV/macaque model provided strong protection against challenge with a pathogenic SIV. Given the urgent need for an HIV vaccine, the potential of this innovative vaccine approach should be evaluated as quickly as possible. Therefore, the aims of the current STREP application of the consortium are 1) to determine the efficacy of the VLPs in a larger number of animals, 2) to better understand the requirements for and the mechanisms of protection, and 3) to further improve the targeted VLPs.

 

Partners

 

Coordinator               Ruhr-University Bochum, Department of Molecular and Medical Virology (Prof. Dr. K. Überla)

Partner 2                   Bernhard-Nocht-Institute for Tropical Medicine (Prof. Dr. P. Racz)

Partner 3                   The Rockefeller-University (Prof. Dr. R. Steinman)

Partner 4                   Innsbruck Medical University (Prof. Dr. H. Stoiber)

Partner 5                   Charité, University Medicine of Berlin (PD. Dr.R.Ignatius)

Partner 6                   Institute for Research in Biomedicine (Dr. M.Uguccioni)

Partner 7                   German Primate Center (Dr. C. Stahl-Hennig)

 

Link to Partner´s Web site: http://134.100.62.15/bni/others/koerber/partner/index.html

 

 

Background

With HIV spreading worldwide, the need for a preventive or therapeutic vaccine is more urgent than ever before. According to the United Nations Program on HIV/AIDS approximately 40 million people worldwide are infected with HIV. No HIV vaccine is yet available. Efficacy studies in humans require large cohorts, and only a single trial using recombinant gp120 surface protein has been performed with no evidence of protection. Therefore, most of our knowledge on HIV vaccines comes from animal models, particularly the infection of macaques with simian immunodeficiency viruses (SIV).

Work on live-attenuated immunodeficiency viruses in non-human primate models has shown that a vaccine can provide protection from progression to AIDS even in the absence of a sterilising immunity. Thus, vaccine-induced antiviral immune responses can control immunodeficiency virus replication. A number of effector mechanisms, including neutralizing antibodies and CD8+ cytotoxic T-cells are likely to contribute to protection. In addition to the live-attenuated vaccines, which for safety reasons are unlikely to be applicable in humans, a number of vaccine approaches have been studied in the SIV model. Vaccination with recombinant env proteins does not provide sufficient protection against pathogenic SIV, which is consistent with results from the human phase-III trial. Similarly, whole inactivated SIV vaccines and virus-like particles do not provide significant protection. A common feature of vaccination with recombinant viral proteins and whole inactivated viruses is injection of exogenous antigens, which predominantly leads to MHC-II-restricted cellular immune responses and production of antibodies. Expression of antigens by cells of the vaccinees should lead to presentation of antigens to MHC-I and MHC-II molecules. Therefore, DNA and viral vector vaccines have been extensively studied and depending on the stringency of the challenge system various degrees of protection have been observed.

Instead of using viral vector systems to induce MHC-I and MHC-II-restricted immune responses, a heterologous fusion protein was incorporated into immunodeficiency  virus-like particles, which should increase uptake and presentation of exogenous antigens on MHC-I and MHC-II molecules. This might explain the initial evidence of protection from disease progression in monkeys immunized with these targeted virus-like particles.

 

 

Consortium

To achieve the objectives, we have endeavoured to put together a consortium of excellence in Europe with a track-record of collaborative research, which can address all relevant issues. Given the important role that dendritic cells play in immunity and therefore in vaccine development, the European partnership is strengthened by an expert on dendritic cells from the USA (Partner 3). The outline below shows the substantial scope of expertises in the consortium, but this scope is essential to approach demanding unknowns in vaccine biology especially in non-human primates. Dr. Klaus Überla (Ruhr-University Bochum, Germany) performs the molecular virology research that provided the basis for the targeted VLPs. His group engineered, produced and characterized the vaccines for the mouse and non-human primate studies. Dr. Ralph Steinman (Rockefeller University, New York, USA) will evaluate the VSV-G targeting efficacy for dendritic cells and requirements and improvements for costimulatory signals to generate mature stimulatory DCs in vivo. The immunogenicity and protective properties of different targeted VLPs will be determined at the German Primate Centre under the direction of Dr. Christiane Stahl-Hennig (German Primate Center, Göttingen, Germany). Dr. Paul Racz  and Dr. Klara Tenner-Racz  (both Bernhard-Nocht-Institute for Tropical Medicine, Hamburg, Germany) will perform molecular pathological analysis of the site of vaccine injection and after challenge in the rhesus monkey model. The analysis of lymphoid tissues is critical to documenting protection at these major sites for viral replication, and to understand mechanisms of protection at the level of T cell and dendritic cell subsets. The molecular pathological analyses will be complemented by a special focus on chemokines, which interact with immune cells as well as virus coreceptors. The question how selected chemokines are involved in the regulation of immune responses and whether they might be directly involved in antiviral effector mechanism will be addressed by Dr. Mariagrazia Uguccioni (Institute for Research in Biomedicine, Bellinzona, Switzerland). Presentation of VLPs by rhesus macaque dendritic cells in vitro and cellular immune responses in blood and lymphatic tissues following vaccination of monkeys and shortly after challenge will be investigated by Dr. Ralf Ignatius (Partner 5). Dr. Heribert Stoiber (Partner 4) will be responsible for analyses of humoral immune responses against viral and cellular proteins.